Interesting Engineering on MSN

First-ever experimental gene therapy seeks to restore vision by rejuvenating eye neurons

Life Biosciences is pushing cellular rejuvenation into the clinic with ER-100, an experimental gene ...
News-Medical.Net on MSN

New workflow boosts nuclear delivery for safer gene therapy

Gene therapy holds the promise of preventing and curing disease by manipulating gene expression within a patient's cells. However, to be effective, the new gene must make it into a cell's nucleus. The ...
Good News Network

Successful World First: Baby Treated with Personalized CRISPR Gene Therapy for Rare Disease is Now ‘Thriving’

Dr. Rebecca Ahrens-Nicklas and Dr. Kiran Musunru crafted a bespoke treatment that has successfully corrected the genetic ...
Monitor

New gene therapy offers hope to sickle cell patients

Gene therapy is a medical treatment that works by changing or fixing a person's genes to treat or prevent disease ...
Audacy on MSN

The story of KJ Muldoon: The baby who received ground-breaking gene-editing therapy at CHOP

VIPs gathered last week for the final beam placement in Children’s Hospital of Philadelphia’s new 26-story tower. But the ...
STAT

FDA halts gene therapy trials after brain tumor found in patient

The Food and Drug Administration paused trials for two experimental gene therapies from Regenxbio after one child developed a ...
News-Medical.Net

First topical CRISPR gene therapy corrects disease-causing mutations in human skin

Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...

Gene-editing therapy proves effective for Leber's hereditary optic neuropathy

A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic ...
Fred Hutch

Scientists see foam as starting point of a path to bedside gene therapy

The special properties of methylcellulose foam could make it a vehicle for bedside genetic engineering, according to a proof-of-principle study from bioengineers at Fred Hutch Cancer Center. In the ...
NC Biotech

AskBio secures IND acceptance for late-onset Pompe disease gene therapy

AskBio Inc., an RTP-based gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, has received U.S. Food and Drug Administration (FDA) acceptance of its ...
Yicai Global

Chinese Scientists Make Key Advance in Using Gene Therapy

(Yicai) Jan. 28 -- Chinese medical researchers have made a breakthrough in gene therapy that overcomes the limitations of ...
MedPage Today on MSN

FDA Halts Two Gene Therapy Trials After Child Develops Brain Tumor

Studies of Hunter and Hurler syndromes on hold ...